Sepideh Zununi Vahed, Mohammadreza Ardalan, Nasser Samadi, Yadollah Omidi* 
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Sina Raeisi, Amir Ghorbanihaghjo*, Hassan Argani, Siavoush Dastmalchi, Babollah Ghasemi, Teimour Ghazizadeh, Nadereh Rashtchizadeh, Mehran Mesgari Abbasi, Nasrin Bargahi, Mahboob Nemati, Ali Mota, Amir Mansour Vatankhah
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Fatemeh Sanie-Jahromi , Masoomeh Eghtedari, Esmaeil Mirzaei, Mohammad Hassan Jalalpour, Zahra Asvar, Mahmood Nejabat* , Fahimeh Javidi-Azad
The represented data indicated the priority of PCL/Gel for LESC attachment, proliferation and transplantation in animal models.
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Mohammad A. Rafi , Paola Luzi, David A. Wenger*
Krabbe disease (KD) is an autosomal recessive lysosomal disorder that imposes defective myelination in the peripheral and central nervous systems. Twitcher combining bone marrow transplantation with AAVrh10-mGALC can have a great extension of life in the murine model of KD.
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Mohammad A Rafi* , Paola Luzi, David A Wenger
Our results demonstrate that, it may be possible to treat human KD patients with high dose AAVrh10 without blood stem cell transplantation which would eliminate the side effects of HSCT.
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Mohammad A. Rafi*
Cutting viral dose in half or using BM cells from heterozygote mice in a combination of BMT and gene therapy treatments result in a similar reduction in lifespan of the treated mice.
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